Patients with rare diseases cannot continue to be overlooked because of costly therapies and have the same rights to treatment as any other patient. At this year's
Orphan Drugs and Rare Diseases conference, taking place on 17 - 18 October in London, industry experts will address the opportunities and challenges within the rare disease treatment field.
Keep up to date with the industry and to learn from expert speaker panel, bringing you important new case studies and reports on this year's relevant topics.
Benefits of Attending
Orphan Drugs and Rare Diseases conference this year is set to inspire the international rare diseases community by exploring synergies between regulators, health and technology assessors
- Discuss strategic win-win collaborations to help accelerate rare disease clinical drug development, and improve relationships between drug developers and patients to consider both parties' interests
- Hear more about how patient engagement by integrating the patient perspective into the drug development process through patient advocacy, patient-centric research and patient groups
- Learn about how the regulatory landscape for drug approvals is different between countries, and why it is important to keep informed about the regulations and guidelines of each region
- Gain knowledge of different rare diseases and their unique challenges, as well as how treatment methods can be transferred to other rare diseases
- Learn how gene therapy methods can improve the treatment of rare diseases and why it is becoming more commercially successful
Plus an Interactive Half-Day Pre-Conference Workshop (PM) | Wednesday 16th October 2018
Working together for HTA in rare diseases - a step too far or the way forward?
Workshop Leader: Josie Godfrey, Director, JG Zebra Consulting
14.00 - 17.00
Speakers
- Alastair Kent, CEO, Genetic Alliance
- Anthony Hall, Therapeutic Area Head Orphan Drugs, Mereo BioPharma
- Carina Schey, Researcher, University Of Groningen
- Michale Bouskila-Chubb, Head of Business Development , Healx
- Neil Dugdale, Vice-President and General Manager, UK and RoI, Sobi
- Nicolas Sireau, CEO and Board Chair, AKU Society
- Nigel Nicholls, Director and Country Manager UK/Ireland, BioMarin Europe Ltd
- Patrick Mollon, Founder and Owner, Mollon Healh-Economics
- Peter Rutherford, Global Medical Lead, Vifor Pharma
- Rizwan Arshad Khan, CEO, Health Services (Pakistan Public Health Association)
- Sheela Upadhyaya, Associate Director - Highly Specialised Technologies , National Institute for Health and Care Excellence
- Sigrid Welte, Founder and General Manager, Pharma Innovation Consultancy GmbH
- Solange Corriol-Rohou, Senior Director Regulatory Affairs and Policy, EU, AstraZeneca
- Toni Mathieson, Chief Executive, Niemann-Pick UK
- Xavier Ortega, Project Manager, Rare Diseases, Minoryx
- Yolanda Barbachano, Senior Statistical Assesor, MHRA
Please fill in your name and email to receive the conference agenda of this event.
Venue
Holiday Inn Kensington Forum
97 Cromwell Rd, Kensington, SW7 4DN
London, UK
Venue
Holiday Inn Kensington Forum97 Cromwell Road
London, United Kingdom
